EP-4493704-A4 - THERAPEUTIC ADENO-ASSOCIATED VIRUS USING CODON OPTIMIZED NUCLEIC ACID ENCODING ALPHA-GLUCOSIDASE (GAA) FOR TREATING POMPE DISEASE, WITH SIGNAL PEPTIDE MODIFICATIONS
EP4493704A4EP 4493704 A4EP4493704 A4EP 4493704A4EP-4493704-A4
Inventors
- TRETIAKOVA ANNA
- ANGUELA MARTINEZ XAVIER
- SUAREZ LESTER
- HAMMOND SCOTT
Assignees
- ASKBIO INC
Dates
- Publication Date
- 20260506
- Application Date
- 20230317
- Priority Date
- 20220318